01.30.20

ProQR Receives Rare Pediatric Disease Designation from FDA for QR-421a

Source: ProQR Therapeutics

10.18.19

ProQR Receives Rare Pediatric Disease Designation from FDA for Sepofarsen for the Treatment of LCA10

Source: ProQR Therapeutics

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FDA Grants Lin BioScience Rare Pediatric Disease Status for LBS-008 to Treat Stargardt Disease

Source: Lin BioScience

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